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Abstract Details

A Pivotal, Randomized, Double-Blind, Placebo-Controlled, Multicenter Trial of N-acetylmannosamine (ManNAc) in GNE myopathy: Results from the NN109 MAGiNE Study
Neuromuscular and Clinical Neurophysiology (EMG)
LS2 - Late-breaking Science 2 (5:45 PM-5:51 PM)
001
Authors/Disclosures
Francis Rossignol, MD, FRCPC
PRESENTER
The institution of Dr. Rossignol has received research support from CRADA between NHGRI, NINDS, NIAMS and Leadiant Biosciences Inc.
Christopher Coffey, PhD, FAAN (University of Iowa) Dr. Coffey has received personal compensation in the range of $5,000-$9,999 for serving as an Editor, Associate Editor, or Editorial Advisory Board Member for American Heart Association. The institution of Dr. Coffey has received research support from NIH. The institution of Dr. Coffey has received research support from Michael J Fox Foundation.
Merit E. Cudkowicz, MD, MSC, FAAN (Massachusetts General Hospital) Dr. Cudkowicz has received personal compensation in the range of $500-$4,999 for serving as a Consultant for biogen. Dr. Cudkowicz has received personal compensation in the range of $0-$499 for serving as a Consultant for cytokinetics. Dr. Cudkowicz has received personal compensation in the range of $0-$499 for serving as a Consultant for immunitypharm. Dr. Cudkowicz has received personal compensation in the range of $500-$4,999 for serving as a Consultant for transposon. Dr. Cudkowicz has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Quralis. Dr. Cudkowicz has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Regeneron. Dr. Cudkowicz has received personal compensation in the range of $500-$4,999 for serving as a Consultant for vectorY. Dr. Cudkowicz has received personal compensation in the range of $500-$4,999 for serving as a Consultant for inflectis. Dr. Cudkowicz has received personal compensation in the range of $500-$4,999 for serving as a Consultant for novartis. Dr. Cudkowicz has received personal compensation in the range of $500-$4,999 for serving as a Consultant for ono. Dr. Cudkowicz has received personal compensation in the range of $500-$4,999 for serving as a Consultant for otsuka. Dr. Cudkowicz has received personal compensation in the range of $500-$4,999 for serving as a Consultant for coya. Dr. Cudkowicz has received personal compensation in the range of $500-$4,999 for serving as a Consultant for ac immune. Dr. Cudkowicz has received personal compensation in the range of $0-$499 for serving as a Consultant for pontifax. Dr. Cudkowicz has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Inflectis. Dr. Cudkowicz has received personal compensation in the range of $0-$499 for serving as a Consultant for ab science. Dr. Cudkowicz has received personal compensation in the range of $500-$4,999 for serving as a Consultant for aclipse. Dr. Cudkowicz has received personal compensation in the range of $5,000-$9,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Locust Walk. Dr. Cudkowicz has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Pasithea. Dr. Cudkowicz has received personal compensation in the range of $50,000-$99,999 for serving as an officer or member of the Board of Directors for Praxis Precision Medicine. Dr. Cudkowicz has received personal compensation in the range of $10,000-$49,999 for serving as an Editor, Associate Editor, or Editorial Advisory Board Member for Annals of Neurology . The institution of Dr. Cudkowicz has received research support from NINDS. The institution of Dr. Cudkowicz has received research support from ALSFAC. The institution of Dr. Cudkowicz has received research support from UCB ra. The institution of Dr. Cudkowicz has received research support from Biohaven. The institution of Dr. Cudkowicz has received research support from Clene nanomedicine. The institution of Dr. Cudkowicz has received research support from prilenia. The institution of Dr. Cudkowicz has received research support from ALS one. The institution of Dr. Cudkowicz has received research support from Seelos. The institution of Dr. Cudkowicz has received research support from Calico. The institution of Dr. Cudkowicz has received research support from denali. The institution of Dr. Cudkowicz has received research support from ITB. The institution of Dr. Cudkowicz has received research support from PharmAust. The institution of Dr. Cudkowicz has received research support from woolsley. Dr. Cudkowicz has received research support from lilly. The institution of Dr. Cudkowicz has received research support from J& J. Dr. Cudkowicz has received publishing royalties from a publication relating to health care.
LUMY SAWAKI-ADAMS (NATIONAL INSTITUTES OF HEALTH) Dr. SAWAKI-ADAMS has received personal compensation in the range of $100,000-$499,999 for serving as a Program Director/Federal Employee with HHS/NIH.
Amy Tsou, MD (National Institute of Neurological Disorders and Stroke) Dr. Tsou has nothing to disclose.
Richard J. Barohn, MD, FAAN (University of Missouri) Dr. Barohn has received personal compensation in the range of $50,000-$99,999 for serving as a Consultant for NuFactor. The institution of Dr. Barohn has received research support from FDA OPD R01. Dr. Barohn has received intellectual property interests from a discovery or technology relating to health care.
Miriam L. Freimer, MD, FAAN (The Ohio State University) Dr. Freimer has received personal compensation in the range of $5,000-$9,999 for serving on a Scientific Advisory or Data Safety Monitoring board for argenx. Dr. Freimer has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for alexion. Dr. Freimer has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for J and J. Dr. Freimer has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for UCB. The institution of Dr. Freimer has received research support from Alnylum. The institution of Dr. Freimer has received research support from UCB. The institution of Dr. Freimer has received research support from NIH. The institution of Dr. Freimer has received research support from Janssen. Dr. Freimer has received research support from Avidity. Dr. Freimer has received research support from Fulcrum. The institution of Dr. Freimer has received research support from Dept of defense. The institution of an immediate family member of Dr. Freimer has received research support from Abcurro. Dr. Freimer has received personal compensation in the range of $10,000-$49,999 for serving as a presentations/teaching with UCB.
Nuria Carrillo, MD Dr. Carrillo has received personal compensation for serving as an employee of Dianthus Therapeutics. Dr. Carrillo has or had stock in Dianthus Therapeutics.Dr. Carrillo has or had stock in Moderna Therapeutics.
Timothy P. Leonard (Massachusetts General Hospital - Neurological Clinical Research Institute) Mr. Leonard has nothing to disclose.
David Klements, MS (Massachusetts General Hospital) Mr. Klements has nothing to disclose.
Dixie J. Ecklund, RN (University of Iowa) The institution of Ms. Ecklund has received research support from NIH. The institution of Ms. Ecklund has received research support from Michael J. Fox Foundation. Ms. Ecklund has received personal compensation in the range of $500-$4,999 for serving as a Scientific Review Board with Department of Defense. Ms. Ecklund has received personal compensation in the range of $500-$4,999 for serving as a Consultant with Northwestern University.
Maxine Koepp Ms. Koepp has nothing to disclose.
Michele Costigan, RN (University of Iowa College of Public Health) Ms. Costigan has nothing to disclose.
Emily Roberts, PhD The institution of Dr. Roberts has received research support from NIH.
Elizabeth Klingner, MS Mrs. Klingner has nothing to disclose.
Charlie Choi The institution of Mr. Choi has received research support from NIH/NINDS. The institution of Mr. Choi has received research support from Michael J. Fox Foundation.
Dosten Kopenhauszen Dosten Kopenhauszen has nothing to disclose.
Melanie Quintana, PhD Dr. Quintana has nothing to disclose.
Farah Khandwala Mrs. Khandwala has received personal compensation for serving as an employee of Berry Consultants, LLC.
Eric Henninger No disclosure on file
William Gahl, MD, PhD The institution of Dr. Gahl has received research support from Leadiant Biosciences. The institution of Dr. Gahl has received research support from NIH. Dr. Gahl has received intellectual property interests from a discovery or technology relating to health care.
Marjan -. Huizing, PhD The institution of Dr. Huizing has received research support from Intramural Research Program NHGRI, NIH. The institution of Dr. Huizing has received research support from CRADA with Leadiant Biosciences. Dr. Huizing has received intellectual property interests from a discovery or technology relating to health care.
Joseph Shrader (NIH) Joseph Shrader has nothing to disclose.
Galen Joe No disclosure on file
Alessandro Noseda, MD Dr. Noseda has nothing to disclose.
Giuseppe Testa, MSc Mr. Testa has received personal compensation for serving as an employee of Leadiant Biosciences, Inc..
Anthony A. Amato, MD, FAAN (Brigham and Women's Hospital) Dr. Amato has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Johnson & Johnson. Dr. Amato has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for argenx. Dr. Amato has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Abcuro. Dr. Amato has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Sanofi. Dr. Amato has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Caballeta. Dr. Amato has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Takeda. Dr. Amato has received personal compensation in the range of $0-$499 for serving on a Scientific Advisory or Data Safety Monitoring board for EMD Serono. Dr. Amato has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Viridian Therapeutics. Dr. Amato has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Medpace. Dr. Amato has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for UCB. Dr. Amato has received personal compensation in the range of $10,000-$49,999 for serving as an Editor, Associate Editor, or Editorial Advisory Board Member for Neurology. Dr. Amato has received personal compensation in the range of $500-$4,999 for serving as an Expert Witness for legal firms. The institution of Dr. Amato has received research support from NIH. Dr. Amato has received publishing royalties from a publication relating to health care.